NHS Scotland has approved a one-time CRISPR gene therapy for severe sickle cell disease, offering durable reduction in vaso-occlusive crises for eligible patients.

CS-101 is Shanghai-based CorrectSequence's lead candidate, which it is developing for treating sickle-cell disease and ...

Sickle cell disease (SCD) is a group of genetic blood disorders. A person inherits SCD from their parents when they inherit two copies of the sickle cell gene, one from each parent. This hereditary ...

If you or someone you know has sickle cell disease (SCD), you may have heard of Lyfgenia, one of two gene therapies approved for this condition. Gene therapies are the only treatments for SCD that can ...

Hoosiers from across the state will gather at the Indiana State Capitol on Monday, Feb. 2, to call attention to the urgent ...

Medicaid is doing a novel payment system for the new, promising and expensive sickle cell treatment. It may become a model ...

Please provide your email address to receive an email when new articles are posted on . Researchers observed what they called “alarming” underutilization of disease-modifying therapies for sickle cell ...

WESTLAND, Mich. — For D’Asia Jackson, every day is a guessing game over whether excruciating pain will upend her life. The 28-year-old medical assistant was born with sickle cell disease, an inherited ...

Sickle Cell Disease (SCD) is a global health challenge that affects millions of people worldwide. Despite significant ...